Metachromatic Leukodystrophy : new therapy advancements and emerging research directions

Asbreuk, Marije A. B. C.; Schoenmakers, Daphne H.; Adang, Laura Ann; Beerepoot, Shanice; Bergner, Caroline; Bley, Annette; Boelens, Jaap Jan; Bugiani, Marianna; Calbi, Valeria; Garcia-Cazorla, Angeles; Eklund, Erik A.; Fumagalli, Francesca; Gronborg, Sabine Weller; Groeschel, Samuel; Van Hasselt, Peter M.; Hollak, Carla E. M.; Jones, Simon A.; de Koning, Tom J.; van Kuilenburg, Andre B. P.; Laugwitz, Lucia; Lindemans, Caroline; Mochel, Fanny; Oberg, Andreas; Ram, Dipak; Schöls, Ludger; Sevin, Caroline; Sinha, Jigyasha; Vaz, Frederic M.; Zerem, Ayelet; Wolf, Nicole I.

Metachromatic Leukodystrophy : new therapy advancements and emerging research directions

Author:

Asbreuk, Marije A. B. C.; Schoenmakers, Daphne H.; Adang, Laura Ann; Beerepoot, Shanice; Bergner, Caroline; Bley, Annette; Boelens, Jaap Jan; Bugiani, Marianna; Calbi, Valeria; Garcia-Cazorla, Angeles; Eklund, Erik A.; Fumagalli, Francesca; Gronborg, Sabine Weller; Groeschel, Samuel; Van Hasselt, Peter M.; Hollak, Carla E. M.; Jones, Simon A.; de Koning, Tom J.; van Kuilenburg, Andre B. P.; Laugwitz, Lucia; Lindemans, Caroline; Mochel, Fanny; Oberg, Andreas; Ram, Dipak; Schöls, Ludger; Sevin, Caroline; Sinha, Jigyasha; Vaz, Frederic M.; Zerem, Ayelet; Wolf, Nicole I.

Tübinger Autor(en):

Groeschel, Samuel
Laugwitz, Lucia
Schöls, Ludger

Published in:

Neurology (2025), Bd. 105, H. 2e213817

Verlagsangabe:

Philadelphia : Lippincott Williams & Wilkins

Language:

English

Full text:

http://dx.doi.org/10.1212/WNL.0000000000213817

ISSN:

0028-3878