Safety and efficacy of leriglitazone in childhood cerebral adrenoleukodystrophy (NEXUS): an interim analysis of an open-label, phase 2/3 trial

Garcia-Cazorla, Angeles; Sevin, Caroline; Constante, Juliana Ribeiro; Yazbeck, Elise; Rosewich, Hendrik; Jimenez, Sandra; Chiang, Gloria Chia-Yi; Rapalino, Otto; Caruso, Paul; Balentine, Daniel; Helmer, Karl G.; Bennett, Seth; Emanuele, Marco; Rodriguez-Pascau, Laura; Pizcueta, Pilar; Pina, Guillem; Vila, Anna; Rovira, Maria; Mantilla, Adriana; Meya, Uwe; Mistry, Arun; Pascual, Maria; Pascual, Silvia; Martinell, Marc; Musolino, Patricia L.; Mallacko, Eric

Safety and efficacy of leriglitazone in childhood cerebral adrenoleukodystrophy (NEXUS): an interim analysis of an open-label, phase 2/3 trial

Autor(en):

Garcia-Cazorla, Angeles; Sevin, Caroline; Constante, Juliana Ribeiro; Yazbeck, Elise; Rosewich, Hendrik; Jimenez, Sandra; Chiang, Gloria Chia-Yi; Rapalino, Otto; Caruso, Paul; Balentine, Daniel; Helmer, Karl G.; Bennett, Seth; Emanuele, Marco; Rodriguez-Pascau, Laura; Pizcueta, Pilar; Pina, Guillem; Vila, Anna; Rovira, Maria; Mantilla, Adriana; Meya, Uwe; Mistry, Arun; Pascual, Maria; Pascual, Silvia; Martinell, Marc; Musolino, Patricia L.; Mallacko, Eric

Tübinger Autor(en):

Rosewich, Hendrik

Erschienen in:

Eclinicalmedicine (2025), Bd. 84, Article 103265

Verlagsangabe:

Amsterdam : Elsevier

Sprache:

Englisch

Referenz zum Volltext:

http://dx.doi.org/10.1016/j.eclinm.2025.103265

ISSN:

2589-5370