CRISPR-Cas9n-mediated ELANE promoter editing for gene therapy of severe congenital neutropenia

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CRISPR-Cas9n-mediated ELANE promoter editing for gene therapy of severe congenital neutropenia

Author: Nasri, Masoud; Ritter, Malte U.; Mir, Perihan; Dannenmann, Benjamin; Kaufmann, Masako M.; Arreba-Tutusaus, Patricia; Xu, Yun; Borbaran-Bravo, Natalia; Klimiankou, Maksim; Lengerke, Claudia; Zeidler, Cornelia; Cathomen, Toni; Welte, Karl; Skokowa, Julia
Tübinger Autor(en):
Nasri, Masoud
Ritter, Malte
Mir, Perihan
Dannenmann, Benjamin
Arreba-Tutusaus, Patricia
Xu, Yun
Borbaran-Bravo, Natalia
Klimiankou, Maksim
Lengerke, Claudia
Zeidler, Cornelia
Welte, Karl
Skokowa, Julia
Published in: Molecular Therapy (2024), Bd. 32, H. 6, S. 1628-1642
Verlagsangabe: Cambridge : Cell Press
Language: English
Full text: http://dx.doi.org/10.1016/j.ymthe.2024.03.037
ISSN: 1525-0016
DDC Classifikation: 570 - Life sciences; biology
610 - Medicine and health
Dokumentart: Article
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