Consensus guidelines for the monitoring and management of metachromatic leukodystrophy in the United States

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Consensus guidelines for the monitoring and management of metachromatic leukodystrophy in the United States

Author: Adang, Laura A.; Bonkowsky, Joshua L.; Boelens, Jaap Jan; Mallack, Eric; Ahrens-Nicklas, Rebecca; Bernat, John A.; Bley, Annette; Burton, Barbara; Darling, Alejandra; Eichler, Florian; Eklund, Erik; Emrick, Lisa; Escolar, Maria; Fatemi, Ali; Fraser, Jamie L.; Gaviglio, Amy; Keller, Stephanie; Patterson, Marc C.; Orchard, Paul; Orthmann-Murphy, Jennifer; Santoro, Jonathan D.; Schoels, Ludger; Sevin, Caroline; Srivastava, Isha N.; Rajan, Deepa; Rubin, Jennifer P.; Van Haren, Keith; Wasserstein, Melissa; Zerem, Ayelet; Fumagalli, Francesca; Laugwitz, Lucia; Vanderver, Adeline
Tübinger Autor(en):
Schöls, Ludger
Laugwitz, Lucia
Published in: Cytotherapy (2024), Bd. 26, H. 7, S. 739-748
Verlagsangabe: London : Elsevier Sci Ltd
Language: English
Full text: http://dx.doi.org/10.1016/j.jcyt.2024.03.487
ISSN: 1465-3249
DDC Classifikation: 570 - Life sciences; biology
610 - Medicine and health
Dokumentart: Article
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